Gene editing to reverse myotonic dystrophy

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Myotonic dystrophy type 1 is a debilitating genetic disease that causes muscle weakness and wasting, amongst other problems, and there's currently no cure. It causes a toxic form of the chemical RNA - a genetic messenger molecule similar to DNA - to build up and clog up other important processes inside cells. Now, scientists at the University of California San Diego have used gene editing to reverse the disease in mice, as Eva Higginbotham heard from Gene Yeo... Like this podcast? Please help us by supporting the Naked Scientists

22 Sep 2020 English United Kingdom Science

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